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Virtual Event

Jun 14, 2020 9:00 AM - Jun 18, 2020 5:00 PM

(Eastern Standard Time)

Fort Washington, PA 19034

DIA 2020 Global Annual Meeting

Non-Profit Organizations Role in Accelerating Preclinical Compound Testing to Fuel the Rare Disease Clinical Pipeline

Session Chair(s)

Daniela  Brunner, PhD

Daniela Brunner, PhD

Founder

Science Forward, United States

A panel will review examples of preclinical drug screening platforms and consortia organized by non-profit organizations. Experts will present their experience and describe the challenges encountered, solutions found, and best practices defined.

Learning Objective : Discuss how rare disease non-profit organizations accelerate drug development; Develop consensus with industry, academia and patients; Identify unmet needs, optimize translational methods, criteria for compound selection, addressing gaps, ensuring quality, reproducibility, robustness and interpretation of data; Discuss challenges and solutions to transparency, data sharing and sustainability.

Speaker(s)

Dean  Aguiar, PhD

Tuberous Sclerosis Complex Preclinical Consortium

Dean Aguiar, PhD

Tuberous Sclerosis Alliance, United States

Director, Preclinical Research

Salvatore  La Rosa, PhD

Panelist

Salvatore La Rosa, PhD

Children's Tumor Foundation , United States

Chief Scientific Officer

Dominique  Pichard, MD

Panelist

Dominique Pichard, MD

Rettsyndrome.org, United States

Chief Science Officer

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