×
Don't Miss Out!
Get your weekly Breakfast Briefing eNewsletter, filled with news, trends, and vital information from DIA!
Back to Agenda
Rare but Real: Navigating Rare Disease Product Development and Market Access Challenges
Session Chair(s)
Representative Invited
DIA, United States
Experts representing industry, non-profit, research, regulatory, and payor perspectives will explore key hurdles and solutions to rare disease treatment development, from recruitment and diagnosis to late-stage development and access after accelerated approval.
Learning Objective : Identify hurdles and solutions to clinical trial recruitment, incl. early diagnosis and newborn screening; Explore approaches to patient stratification, disease understanding, and novel biomarkers, while de-risking late-stage development in competitive and high-failure landscapes; Examine challenges of market access and pricing after accelerated approval, and gain insights into addressing payer-specific concerns to ensure equitable access.
Speaker(s)
Panelist
Annie Kennedy
EveryLife Foundation for Rare Diseases, United States
Chief of Policy, Advocacy, and Patient Engagement
Have an account?