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Omni Shoreham Hotel

22 ene 2018 7:00 a.m. - 24 ene 2018 5:00 p.m.

2500 Calvert Street NW, , Washington, DC 20008 , USA

Pharmacovigilance and Risk Management Strategies Conference

Opening Keynote: Patient Advocacy in Rare Disease: Duchenne Muscular Dystrophy

Session Chair(s)

William  Gregory, PhD

William Gregory, PhD

Senior Director, Safety and Risk Management

Pfizer Inc, United States

Rare diseases present special challenges for patients, caregivers, and those who seek to develop and provide safe and effective treatments. One disease that presents such challenges is Duchenne Muscular Dystrophy (DMD), a genetic disorder that is characterized by progressive muscle degeneration and weakness caused by an abnormality in the dystrophin complex in muscle fiber. Development of safe and effective biopharmaceutical interventions has been enigmatic. This session will provide an overview of this devastating disease, patient advocacy efforts, and the partnership network that has emerged to facilitate development of evidence-based interventions.

Speaker(s)

Christine  McSherry, BSN, RN

Speaker

Christine McSherry, BSN, RN

Casimir LLC, United States

Chief Executive Officer

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