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Capital Hilton

28 oct 2024 8:30 a.m. - 30 oct 2024 12:40 p.m.

1001 16th Street NW, Washington, DC 20036-5794

DIA/FDA Oligonucleotide-Based Therapeutics Conference

Session 10 Track 1: Clinical Pharmacology of Oligonucleotides

Session Chair(s)

Hobart  Rogers, PharmD, PhD

Hobart Rogers, PharmD, PhD

Pharmacologist

FDA, United States

Mark  Rogge

Mark Rogge

Adjunct Professor

University of Florida, United States

This session will explore the various clinical pharmacology aspects that are primarily unique to RNA-oligonucleotides. Topics will include: regulatory considerations regarding clinical pharmacology studies, transitioning to first-in-human studies, and the importance of pharmacodynamic biomarkers. Overall, this session will provide various viewpoints on the unique challenges encountered in the clinical development of oligonucleotides.

Learning Objective : At the conclusion of this session, participants should be able to:
  • Distinguish between EMA and FDA Clinical Pharmacology Guidelines in relation to oligonucleotides
  • Recognize the various challenges in the development of pharmacodynamic biomarkers in clinical studies
  • Appraise the clinical pharmacology issues unique to oligonucleotides compared to small molecules and biologics

Speaker(s)

Carolien  Versantvoort, PhD

An Overview of EMA’s Clinical Pharmacology Assessment of Oligonucleotides

Carolien Versantvoort, PhD

Medicines Evaluation Board, Netherlands

Senior Clinical Pharmacokinetics Assessor

Hobart  Rogers, PharmD, PhD

Clinical Pharmacology Aspects of Oligonucleotides

Hobart Rogers, PharmD, PhD

FDA, United States

Pharmacologist

Xiao  Hu, PhD, MSc

Application of Model Informed Drug Development in Clinical Pharmacology for Oligonucleotides

Xiao Hu, PhD, MSc

Wave Life Sciences, United States

Vice President, DMPK and Clinical Pharmacology

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